Gene therapy introduces functional copies of genes to compensate for abnormal disease-associated genes and holds great promise for treating a variety of inherited genetic disorders. Recently, new advances in gene therapy combine regenerative approaches. Scientists working in regenerative gene therapy grow functional forms of cells or tissue to replace damaged ones. In this webinar, researchers will discuss how gene therapy has been used to treat disease and new research approaches to regenerative gene therapy.

Topics to be covered

• Lentivirus-mediated gene therapy for Fabry disease
  
• Combining stem cell and gene therapy to mitigate Huntington’s disease symptoms

Speaker Information: